Scientists use CRISPR/Cas9 to display the highest efficiency yet in correcting the mutation that leads to sickle cell in human hematopoietic stem cells. These cells, when transplanted into modified mice cure the disease. Human clinical trials are planned.

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Scientists use CRISPR/Cas9 to display the highest efficiency yet in correcting the mutation that leads to sickle cell in human hematopoietic stem cells. These cells, when transplanted into modified mice cure the disease. Human clinical trials are planned.